American journal of ophthalmology۲٬۰۲۶نمایه شده در PubMed
Xue Han, Zhaoqi Zhu, Ziyue Song, Gaoqin Liu, Xue Yin, Jiawei Shen, Junfa Xue, Kai Wu, Xueting Luo, Zhiping Cui, Peirong Lu
چکیده
To evaluate the safety, tolerability, and preliminary efficacy of a single intravitreal injection of UGX-201, an optogenetic therapy utilizing an adeno-associated virus 2 type 7m8 variant to deliver a recombinant chimeric opsin to retinal ganglion cells, in advanced nonsyndromic retinitis…
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DOI: 10.1016/j.ajo.2026.03.042