Investigative ophthalmology & visual science۲۰۲۵نمایه شده در PubMed
Xing Wei, Sisi Ma, Yunyu Zhou, Haoliang Cui, Shan Zhang, Duanyang Wang, Yingying Fu, Wei Li, Huihui Han, Yamei Li, Wuyi Li, Huixin Liu, Zixi Sun, Xiaoxu Han, Xuan Zou, Hui Li, Cheng Wang, Ruifang Sui
چکیده
X-linked juvenile retinoschisis (XLRS) is a retinal disease caused by retinoschisin 1 (RS1) gene variants, potentially leading to severe visual impairment and blindness. This study aimed to develop a novel adeno-associated virus (AAV) serotype and evaluate its therapeutic potential in an XLRS mouse…
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DOI: 10.1167/iovs.66.4.37