Eye (London, England)۲۰۲۶نمایه شده در PubMed
Peter Kiraly, Tsveta Ivanova, Assad Jalil
چکیده
Voretigene neparvovec (VN) improves retinal sensitivity in biallelic RPE65-associated inherited retinal dystrophy (IRD), with greater best-corrected visual acuity (BCVA) gains reported in children. We describe a 13-year-old male with biallelic RPE65-IRD who underwent bilateral VN treatment without…
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DOI: 10.1038/s41433-026-04830-5